Oun Al-iedani1,2, Saadallah Ramadan2,3, Karen Ribbons2, Rodney Lea2, and Jeannette Lechner-Scott2,4,5
1School of Health Sciences, University of Newcastle, Newcastle, Australia, 2Hunter Medical Research Institute, Newcastle, Australia, 3Faculty of Health and Medicine, University of Newcastle, Newcastle, Australia, 4Department of Neurology, John Hunter Hospital, Newcastle, Australia, 5School of Medicine and Public Health, University of Newcastle, Newcastle, Australia
Synopsis
This novel study
compares the neurometabolic effects of different DMTs on the MS brain. We
evaluated volumetric and neurometabolic changes in RRMS patients on fingolimod(N=52),
injectables(N=46) and HCs cohort(N=51). MRS was acquired from PCG and PFC. Compared
to HCs, a significant reduction in NAA/tCr were detected in both locations and cohorts.
Clinical parameters, MR-volumetrics and neurometabolic concentrations showed no
statistically significant differences between RRMS cohorts. MRI metrics and
neurometabolites from both locations, showed moderate correlations with cognition,
fatigue and memory. This the first study demonstrating
that fingolimod and injectable DMTs influence volumetric and neurometabolic
profiles of MS-brain similarly.
Background
Disease modifying therapies
(DMTs) can reduce the frequency of relapses and mitigate the long-term damage
caused by these relapses in multiple sclerosis (MS) patients. Therapeutic
trials using MRI have demonstrated the efficacy of many DMTs including
injectable therapies like glatiramer acetate (GA) and interferon (IFN-b) and
oral treatment like fingolimod in relapse-remitting MS (RRMS) by demonstrating
reduced MRI- activity1,2 .However, MRI
features of MS are not specific to its pathological substrates leading to permanent
disability.
Treatment response
studies using a novel proton magnetic resonance spectroscopy (H-MRS) have
demonstrated a significant increase in N-acetylaspartate/total creatine (NAA/tCr)
in RRMS patients and reduction in fatigue symptoms of GA therapy 3-5. Fingolimod has shown
a clear benefit in preventing brain atrophy early 6, which has always
been associated with lower cognitive decline. However, to date, the in-vivo
human impact of MS treatments on pre-frontal cortex (PFC) and Posterior
cingulate gyrus (PCG) metabolism has not been evaluated.
To our knowledge this
is the first study to compare the neurometabolic effects of different DMTs on
the MS brain. In particular, we evaluated volumetric and neurometabolic changes
in RRMS patients on fingolimod or injectables and compared these to a matched
healthy cohort(HCs).Materials and Methods
A total
of 98 RRMS patients aged between 20 to 55 years were on fingolimod (N=52) and
(INF-b or GA,N=46). HCs (N=51) were age and sex matched to the RRMS cohort. All
MRI/MRS were undertaken on a 3T (Prisma, Siemens) MRI scanner equipped with a
64 channel coil. Patients were on treatment for at least 6 months and had EDSS
< 4. All patients underwent cognitive, fatigue and mental health assessment
as well as EDSS.
Structural
imaging using 3D T1-MPRAGE (TR/TE/TI=2000/3.5/1100 ms, 7° flip angle,
FOV=256x256mm2, voxel size:1mm3) as well as 3D T2-FLAIR
(TR/TE/TI=5000/386/1800ms, 12° flip angle, FOV=256x256 mm2, voxel
size: 1mm3) were acquired.H-MRS was applied using a Point RESolved
Spectroscopy (PRESS) sequence acquired from PCG and PFC regions (Figure 1) with
the following acquisition parameters:TR/TE=2000/30ms, PCG voxel size =30x30x30
mm3,PFC voxel size =15x15x15 mm3, averages= 96 and water
suppression was enabled.
FSL and
SPM12 were used for total brain volume, grey matter (GM), white matter (WM),
CSF volumes and segmentation of lesion and MRS voxels7-9. Volumetric metrics and Lcmodel
neurometabolic ratios were compared in the three cohorts using a univariate
general linear model. Correlations of the above MR metrics with clinical
severity and neuropsychological scores were also performed using non-parametric
correlations. Results
Demographic and clinical
parameters of study cohorts are shown in Table 1. Individual and combined RRMS
cohorts showed similar statistically significant volumetric differences: GM
(-3%), WM (-5%) and CSF (+40%) compared to HCs. Both RRMS cohorts showed no
differences were detected in PCG and PFC voxels composition. Using single voxel
H-MRS, compared to HCs, a reduction in NAA/tCr in PCG (-7%, p=0.001) and PFC
(-9%, p=0.001) were detected in both cohorts (fingolimod and injectable)(Figure
3). In PFC, an increase in myo-inositol (m-Ins)/tCr (+5%, p=0.03) were also
detected in both cohorts (Figure 3).
Clinical parameters, MR
volumetrics and neurometabolic concentrations showed no statistically
significant differences between the fingolimod and injectable cohorts. PCG-glutathione (GSH), m-Ins and total choline(tCho) displayed a negative correlation with total
audio recorded cognitive screen (tARCS)
(|r| ≤ 0.446), while GSH and tCho showed a negative correlation with symbol digit
modalities test (SDMT) (|r| ≤ 0.395). In PFC, GSH and Glx were
negatively correlated with anxiety and depression (|r| ≤ 0.351) (Table 2).
Including volumetric
parameters, NAA was negatively correlated with the Modified
Fatigue Impact Scale (MFIS) (r=-0.315) and CSF volume (r=-0.425) (Table 2).Discussion
In this study we confirm
significant neurometabolic and volumetric differences between MS patients and
HCs 10-12. The surprising finding of this study is, that we did not find a difference
between patients treated with the high efficacy treatment fingolimod and
patients treated with injectables. We found significant correlations of many of
our metabolites with clinical outcomes. However, only PCG NAA levels correlated
negatively with higher CSF volume, reinforcing the role of NAA as a marker for
neuronal integrity, and a more sensitive marker of brain atrophy. We observed a
negative correlation between the PCG NAA levels and MFIS as well as CSF volume
in RRMS, which disagrees with other work 13.Studies in MS have shown that changes to PCG and PFC may be sensitive to
the progression of clinical and cognitive disabilities of MS patients and may
play an important role in the improvement of cognitive performance 14,15.Conclusion
The current study is the first cross-sectional in-vivo investigation
comparing the impact of fingolimod, interferon or GA treatments on the PFC and
PCG metabolism in RRMS patients. We demonstrated that fingolimod and injectable
DMTs influence volumetric and neurometabolic profiles of MS brain similarly.
Longitudinal studies are required to further clarify metabolic differences over
time, and to determine an association between brain metabolism and treatment
efficacy. However, our findings suggest that MRS of neurometabolites in these
regions are more sensitive markers than morphological changes.Acknowledgements
Funding for this study provided by Novartis Pharmaceuticals Australia.
The authors thank the patients and controls who participated in this study and the Imaging Centre of the University of Newcastle and Hunter Medical Research Institute.
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