Lindsay Kathleen Hill1,2,3, Che Fu Liu3, Teeba Jihad3, Youssef Zaim Wadghiri2, and Jin Kim Montclare3,4
1Biomedical Engineering, SUNY Downstate Medical Center, Brooklyn, NY, United States, 2Radiology, New York University School of Medicine, New York, NY, United States, 3Chemical and Biomolecular Engineering, New York University Tandon School of Engineering, Brooklyn, NY, United States, 4Chemistry, New York University, New York, NY, United States
Synopsis
Our goal is to create protein engineered biomaterials for dual drug delivery and MRI monitoring to improve the growing field of theranostics. Here we present a drug binding protein that is templated to USPIOs using a biomineralization-inspired biotemplation method. The agent shows promise for T2/T2*-weighted MRI.
Introduction
In the growing field of theranostics, combining
imaging with drug therapy, image-ready multifunctional biomaterials could greatly
advance the way we treat diseases including cancer. Our work aims at coupling MRI
and protein engineering to generate trackable therapeutic platforms rationally
designed on the genetic level with controlled assembly. Our therapeutic system
is based on a coiled-coil protein Q, maintaining a hydrophobic pore for binding
small molecules, such as anti-neoplastic curcumin. Q has been engineered to
maintain charged surface patches for nanofiber assembly and, upon curcumin
binding, fluorescent micron-scale constructs1.
For diagnostic purposes, we exploited ultrasmall
superparamagnetic iron oxide particles (USPIOs) due to their high sensitivity and
tolerance in vivo. USPIO synthesis, however, often consists of harsh conditions
followed by surface coating and additional functionalization. To avoid these
methods, we take advantage of a CMms6 peptide, derived from the C-terminus of
the iron templating protein Mms6 of magnetotactic bacteria2. Mms6 binds and
organizes iron oxide (magnetite) particles, without subsequent surface
alterations. Using azide-alkyne functionalization, an alkyne-functionalized
CMms6 is covalently conjugated to an azide-functionalized variant of Q. By
linking curcumin-carrying Q to CMms6, we have created a drug carrying scaffold capable
of templating and organizing USPIOs called USPIOH, for USPIO-hybrid
biomaterial, for small molecule delivery monitored via T2/T2*-weighted MRI.Methods
Synthesis: Wild type and azide-functionalized Q were
expressed in methionine auxotrophic E. coli M15MA. Using residue-specific incorporation
of non-natural amino acid azidohomoalanine, azide-functionalized Q was produced3.
Purified proteins were dialyzed into acidic buffer initiating nanofiber
assembly and subsequently bound to curcumin1, forming drug-carrying micron-scale
constructs then chemically crosslinked for stability. Crosslinked
constructs were covalently attached to an alkyne-funtionalized CMms6 via azide-alkyne
cycloaddition4 to link Q to USPIOs, forming USPIOH (Figure 1a).
USPIOs were synthesized via room
temperature (RT) co-precipitation of FeCl3 and FeCl2 by NaOH in the absence or presence
of CMms6, Q-CMms6, or wild type Q incapable of conjugating CMms6. For validation,
our protein-mediated USPIO synthesis was compared to a traditional high
temperature reaction in which iron oxide was precipitated and mixed at 85°C5.
Characterization:
Transmission electron microscopy
(TEM, JEM-1400, JEOL) assessed protein nanofiber assembly and USPIO organization.
Electron diffraction rings allowed for the calculation of USPIO d-spacing to confirm magnetite
composition. Fluorescence and bright-field microscopy (DMI4000 B, Leica) was
used to assess micron-scale protein constructs.
MRI:
MRI sequences were evaluated on a 7T Bruker
micro-MRI using degassed 2% agarose phantoms containing known amounts of iron
oxide samples, including clinically-used Feraheme for comparison. Relaxivity
values were assessed using 2D relaxation maps and mono-exponential fitting of the
time points acquired. To quantify T1, T2, and T2* times, we used a Look-locker
sequence with TE=8.92ms-12.608s, a multi-slice multi-echo sequence with
TE=11.034ms-706.176ms, and a multi-gradient echo sequence with
TE=2.8ms-60.25ms, respectively. A T1-weighted image was also acquired at
TR=150ms to visualize the samples’ T1 effect.
Results
TEM of azide-functionalized Q prior to
curcumin-binding revealed nanofibers averaging 128.2nm ±137.7nm, N=33 (Figure 1b). Following
curcumin-binding and crosslinking, fluorescence microscopy showed micron-scale assembly
averaging 25.7µm ±12.7µm diameter, N=72 (Figure 1c). After cycloaddition to
CMms6 and USPIO templation, bright field microscopy of USPIOH suggested that mesofibers
were coated in USPIOs (Figure 1d).
TEM of iron oxide confirmed that in the absence
of CMms6, USPIOs are not formed at RT (Figure 2b,d). However, CMms6 organized
USPIOs (Figure 2b) with a diameter of 18.01nm ±4.05nm, N=40 (Figure 2c). Q-CMms6 organizes USPIOs (USPIOH) averaging
16.88nm ±3.74nm, N=40 (Figure 2e). Diffraction rings of USPIOs templated by
CMms6 and Q-CMms6 (Figures 3a and 3b) revealed d-spacing in agreement with that of well-described magnetite6,
confirming their magnetite composition.
T1, T2, and T2*-weighted MRI (Figure 4) showed
that RT iron oxide in the absence of CMms6 causes minimal signal change in all
three sequences, perhaps due to its lack of organization as demonstrated on TEM
(Figure 2a). While all house-made constructs showed minimal T1 effect, Q-CMms6-templated USPIOH sample performed better as a T2/T2* agent than iron oxide synthesized in
the absence of protein at RT and 85°C, and it maintained
a 7.4-fold higher r2/r1 than Feraheme (Figures4 and 5). Discussion
By biologically synthesizing a coiled-coil
protein and utilizing bio-inspired iron oxide templation, we engineered a trackable
USPIO-functionalized drug-carrying hybrid scaffold, USPIOH. TEM studies
confirmed that its ability to organize USPIOs is due to conjugation to
iron-templating CMms6 and MRI studies revealed that organized USPIOs are
necessary for appreciable relaxation effect. Our USPIOH was validated by its higher
relaxivities than the well-established high temperature USPIO synthesis method
and its 7.4-fold higher r2/r1 than Feraheme, suggesting its use as a
theranostic agent enabling chemotherapeutic delivery to be visualized via
T2/T2*-weighted MRI. Acknowledgements
This work was supported by ARO (W911NF-11-1-0449) and NSF MRSECProgram award number DMR-0820341.References
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