Isaac Mawusi Adanyeguh1, Emilie Poirion1, Daniel GarcĂa-Lorenzo2, Marie-Stephane Aigrot1, Brahim Nait-Oumesmar1, Boris Zalc1, Alexandra Petiet1,2, and Bruno Stankoff1,3
1Inserm U 1127, CNRS UMR 7225, Sorbonne Universités, UPMC Univ Paris 06 UMR S 1127, Brain and Spine Institute, ICM, F-75013, Paris, France, Paris, France, 2Center for NeuroImaging Research (CENIR), Brain and Spine Institute, 75013 Paris, France, Paris, France, 3AP-HP, Saint Antoine Hospital, Department of Neurology, 184 bd Faubourg Saint Antoine, 75012 Paris, Paris, France
Synopsis
Endogenous remyelination can potentially restore
rapid axonal-conduction and confer neuroprotection in chronic demyelinating
diseases such as multiple sclerosis. We used T2 mapping to evaluate
the ability of two candidate pharmacological agents to promote remyelination in
cuprizone-demyelinated mice. Demyelination was associated with increase in signal
intensity and T2 values in the corpus callosum and external capsules.
T2 values showed spontaneous
recovery after discontinuation of cuprizone
treatment, an effect accelerated following administration of the two compounds
tested. This
study confirms that in vivo MRI can
be used to select pharmacological agents for their therapeutic potential on
remyelination.Purpose
Loss of myelin is a major pathological
hallmark of multiple-sclerosis (MS) lesions. Remyelination is a regenerative
process that can restore saltatory conduction and protect axons from
degeneration.
1 There is a crucial need for the development of potential
drugs that could enhance and/or accelerate remyelination in patients with MS. The
aim of this study was to assess the ability of ultra-high field MRI to quantify
the effect of candidate pro-myelinating compounds on spontaneous remyelination
in the cuprizone mouse model.
Methods
Cuprizone ingestion
induces oligodendrocyte cell death in mice, and demyelination that predominates
in the corpus callosum also affects cerebellar peduncles, external capsules,
and grey matter.2,3,4 We hypothesized that 11.7 T MRI could evaluate
in vivo the efficacy of candidate
molecules on remyelination in white matter. The tocopherol derivative, TFA-12,
previously shown to promote oligodendrocyte regeneration in EAE and
lysolecithin-demyelinated mouse models of MS5 and a novel candidate
molecule that promotes oligodendrocyte differentiation were evaluated. We
focused on the caudal corpus callosum (CC), rostral corpus callosum (RC) and
the external capsule (EC) since we have previously shown that MRI was sensitive
enough to capture demyelination and remyelination in these regions.6
a) Mouse Model: Eighteen C57BL6 female mice (8 weeks old)
were fed 0.2% cuprizone for 12 weeks. The animals were then divided into three
groups and fed normal chow afterwards. The TFA-12 group (n = 5) was given intra-peritoneal
injection of 0.39 mg/kg TFA-12 daily. The second group (n = 7) was treated daily
with intra-peritoneal injection of the novel candidate drug. The control group
(n = 6) received daily dose of saline solution.
b) MRI Experiment: All images were acquired on an 11.7 T MRI
system (Bruker Biospec 117/16 USR, 750 mT/m gradients, PV5.1) using a CryoprobeTM
as previously described.6 The animals were imaged before and after
being fed cuprizone (pre-visit and day 0 respectively), and then 15, 30 and 45
days whilst being fed normal chow and receiving treatment. T2-weighted
brain images were acquired with 2D RARE sequence (TR = 6000 ms, TE = 40 ms, resolution
= 60 x 60 μm2, slice thickness =
220 μm) to follow the demyelination. Parametric
T2 maps were obtained from a MSME sequence (TR = 5500 ms, TE = 15-120 ms/15
ms increments, matrix = 128 x 128, resolution = 100 x 100 μm2, slice thickness = 200 μm). The quantitative values obtained from T2
maps compared to visual assessment of T2-weighted images make T2
mapping an important quantitative tool to evaluate changes in brain structure.
c) Data extraction and analysis: T2 values were calculated from
a regression fit function from the multi-echo sequence using the Paravision 5.1
image sequence analysis. Using anatomical landmarks, regions of interest were manually
drawn on 3 consecutive slices and averaged to get the T2 values in
the CC, RC and EC. Analysis of variance (ANOVA) was used to test for
significance (p < 0.05) with step-down Bonferroni correction.
Results and Discussion
T2 RARE images
showed prominent hyper-intensities in the CC (Fig 1b), RC (Fig 1d, red arrow), and
EC (Fig 1d, green arrow) after cuprizone diet compared to the pre-cuprizone
condition (Fig 1a and 1c), characteristic of demyelination.
The
parametric T2 maps showed an increase in the T2 values
after 12 weeks of being fed cuprizone diet. After cessation of cuprizone
administration, the T2 values began decreasing, with an accelerated
recovery in the EC on day 15 for both treatments and on day 30 for the novel
agent (p < 0.05). This suggests that the pro-myelinating drugs have the
potential to accelerate recovery from demyelination.
Comparing the successive time-points
within each group, we observed that when compared to day 0, the decrease in T
2
values was significant as soon as day 15 and remained significant up to day 45
in the treatments groups (p < 0.05), whilst in the control group, it was
only significant in RC and EC from day 30 (p < 0.05). This further supports
that the pharmacological agents accelerate the recovery process.
Conclusion
Ultra-high field MRI had the sensitivity
to quantify
in vivo the impact of two
candidate compounds for enhancing myelin repair. This technique might be used
for the preclinical selection of candidate promyelinating drugs before their
translation into early phase clinical trials.
Acknowledgements
Program
“Investissements d’avenir” ANR-10-IAIHU-06. Ile-de-France
Region (DIM Cerveau et Pensée).
References
1. Irvine KA, Blakemore
WF. Remyelination protects axons from demyelination-associated axon
degeneration. Brain 2008;131:1464 -1477.
2. Cammer W. The
neurotoxicant, cuprizone, retards the differentiation of oligodendrocytes in
vitro. J Neurol Sci. 1999;168(2):116-120.
3. Benardais K, Kotsiari A, Skuljec J, et al. Cuprizone [bis(cyclohexylidenehydrazide)]
is selectively toxic for mature oligodendrocytes. Neurotox Res. 2013;
24(2):244-250.
4. Ransohoff RM.
Animal models of multiple sclerosis: the good, the bad and the bottom line. Nat
Neurosci. 2012;15(8):1074-1077.
5. Blanchard B, Heurtaux T, Garcia C, et al. Tocopherol Derivative TFA-12 promotes
myelin repair in experimental models of multiple sclerosis. J Neurosci.
2013;33(28):11633-1642.
6. Petiet
A, Aigrot MS, Stankoff B. Gray matter
demyelination and remyelination detected with multimodal quantitative analysis
at 11.7T in a mouse model of multiple
sclerosis. ISMRM proceedings 2014.