Intra and inter-tumor heterogeneity pose a challenging task for predicting tumor behavior due to the limited understanding of the molecular mechanism of clear cell renal cell carcinoma (ccRCC) development. The purpose of the present study was to correlate non-invasive quantitative measures of heterogeneity on MR imaging with histopathologic signatures of aggressiveness and gene expression heterogeneity in ccRCC. MRI derived Haralick texture features offer objective, quantitative measures of ccRCC aggressiveness, which can help compensate for the limitations of percutaneous biopsies in the tissue characterization of larger, heterogeneous tumors and assist in the implementation of active surveillance and neoadjuvant therapy protocols.
Introduction: Clear cell renal cell carcinoma (ccRCC) represents the most common and aggressive subtype of RCC (65%–70%) and is highly variable in prognosis, biology, and therapy response [1-3]. Intratumoral heterogeneity (ITH) relates to aggressiveness in ccRCC [4]. Although percutaneous biopsies have high diagnostic accuracy for malignancy, reliability for tumor grading suffers in larger masses due to ITH . Noninvasive in vivo quantitative magnetic resonance imaging (MRI) methods that provide an objective, quantitative assessment of ITH in the whole tumor are therefore appealing. Haralick texture features extracted from a gray level co-occurrence matrix (GLCM) is a robust method to assess intrinsic tumor imaging characteristics [5]. Some of these features, including entropy (measure of ITH), have recently been used in differentiating malignant lesions from benign tumors in various organs. We aim to understand how tumor entropy extracted from MRI correlate with tumor grade and gene expression heterogeneity in ccRCC.
Material and Methods: This IRB-approved, prospective, and HIPAA- compliant study included 62 patients with ccRCC between 2012 - 2017 who signed a written informed consent prior to MRI. MRIs were performed on a 3T whole body MRI system (Ingenia, Philips Healthcare) using dStream anterior and posterior torso coils. Axial and coronal T2-weighted (T2W) ((TR/TE) = 1115/80ms, flip angle (FA) = 90o, number of signal averages (NSA) = 1, slice thickness = 5 mm, field of view (FOV) = 402 x 340 mm2, matrix = 284 x 268, bandwidth = 467 Hz per pixel) anatomic images were acquired. Pseudo-continuous ASL (pCASL) MRI was performed with TR of 6 seconds to allow a complete recovery of the spin magnetization and allow for guided breathing. Sixteen label and control pairs for the ASL were acquired and averaged. A proton density-weighted image (M0) was also acquired without the labeling or background suppression for perfusion quantification [6]. All tumors were manually segmented by an expert radiologist on OsiriX MD DICOM viewer. A region of interest (ROI) was drawn to include the entire tumor avoiding the contour of the lesion to minimize partial volume effects. An OsiriX-based plugin (pyOsiriX) and an open-source Python library (Mahotas) were used to perform the texture analysis [7,8]. A GLCM was constructed for each ROI and 13 Haralick texture features were calculated. After surgery, tumors were graded per International Society of Urological Pathology (ISUP) grading system. RNA extraction from 182 tumor samples in 49 surgically resected tumors were performed according to established protocols [9]. Library preparation (Illumina TruSeq mRNA Library Kit) and mRNA sequencing (HiSeq 4000) were done (Admerahealth, South Plainfield, NJ) (Schematic, Fig 1).
Statistical Analysis: Correlation between texture features and tumor grade was evaluated by logistic regression and area under the ROC curve (AUC). Entropy was correlated with standard deviation (SD) of normalized gene expression levels in multiple samples from the same tumor and Spearman correlation (rho) was computed for each gene. False discovery rate (FDR) (q-values) of < 0.05 considered statistically significant. Softwares: SAS 9.4 (SAS Institute, NC) and R (R Foundation for Statistical Computing, Austria).
Results: Entropy was higher in high-grade than low-grade tumors on T2W (q = 0.028) and ASL (q = 0.04) (Fig 2). Entropy had an AUC of 0.70 (T2) for high-grade prediction and was weakly correlated with tumor size (R2 = 0.2) (Fig 3). Higher T2 and ASL entropy correlated with higher variability in gene expression (Fig 4). Gene ontology analysis of top correlated genes revealed strong enrichment of genes in metabolic processes suggesting higher heterogeneity in tumor perfusion correlates with increased heterogeneity in the expression of metabolic genes. Further, Gene Set Enrichment Analysis performed on the top genes positively correlated with ASL-Entropy showed significant enrichment of hallmark pathways implicated in ccRCC tumorigenesis (Fig 5).
Conclusion: Correlation between higher entropy on MRI and both higher tumor grade and increased gene expression heterogeneity in ccRCC suggest that the imaging phenotype may reflect the marked molecular heterogeneity that characterizes ccRCC. While the safety (i.e. low risk of developing metastases) of AS in larger tumors (cT1b/T2) has been documented, the reliability of tumor biopsies to accurately grade RCC is limited. Lack of reliable predictors of oncologic behavior represent an important argument for resistance to using AS in these larger tumors. An imaging biomarker that provides accurate information about tumor biology/aggressiveness non-invasively (e.g. Haralick texture features) in the whole tumor could overcome these limitations and would facilitate the adoption of AS in these patients. Furthermore, the non-invasive assessment of ITH may facilitate selection of patients for neoadjuvant therapy protocols.
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